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bioRxiv · 10.1101/2024.06.02.597018

Predicting binding events in very flexible, allosteric, multi-domain proteins

Abstract

Knowledge of the structures formed by proteins and small molecules is key to understand the molecular principles of chemotherapy and for designing new and more effective drugs. During the early stage of a drug discovery program, it is customary to predict ligand-protein complexes in silico, particularly when screening large compound databases. While virtual screening based on molecular docking is widely used for this purpose, it generally fails in mimicking binding events associated with large conformational changes in the protein, particularly when the latter involve multiple domains. In this work, we describe a new methodology to generate bound-like conformations of very flexible and allosteric proteins bearing multiple binding sites by exploiting only information on the unbound structure and the putative binding sites. The protocol is validated on the paradigm enzyme adenylate kinase, for which we generated a significant fraction of bound-like structures. A fraction of these conformations, employed in ensemble-docking calculations, allowed to find native-like poses of substrates and inhibitors (binding to the active form of the enzyme), as well as catalytically incompetent analogs (binding the inactive form). Our protocol provides a general framework for the generation of bound-like conformations of challenging drug targets that are suitable to host different ligands, demonstrating high sensitivity to the fine chemical details that regulate proteins activity. We foresee applications in virtual screening, in the prediction of the impact of amino acid mutations on structure and dynamics, and in protein engineering.

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BibTeXRIS

Basciu, A., Athar, M., Kurt, H., Neville, C., Malloci, G., Muredda, F., Bosin, A., Ruggerone, P., Bonvin, A., Vargiu, A. V.. 2024-06-03. Predicting binding events in very flexible, allosteric, multi-domain proteins. https://doi.org/10.1101/2024.06.02.597018

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