@misc{indiciaea0fdc5cb666b, title = {RAPTOR-targeted Antisense Oligonucleotides Restrict Pathological mTORC1 Activity in GATOR1-dependent Disease}, author = {Hadj-Aissa, I. and Muller, M. and Desmeules, A. and Marcadet, L. and Lachance-Brulotte, T. and Morin, N. and Huot, M.-E. and Soliz, J. and Sephton, C. F. and Dutchak, P. A.}, year = {2026}, doi = {10.64898/2026.09.30.755052}, url = {https://www.biorxiv.org/content/10.64898/2026.09.30.755052v1}, note = {Source identifier: 10.64898/2026.09.30.755052} }