TY  - RPRT
TI  - KLHL40 gene replacement therapy in severe nemaline myopathy improves survival and skeletal muscle function in a preclinical mouse model
AU  - Tate, G. R.
AU  - McNulty, J.
AU  - Widrick, J.
AU  - Gupta, V. A.
PY  - 2026
DO  - 10.64898/2026.09.23.753846
UR  - https://www.biorxiv.org/content/10.64898/2026.09.23.753846v1
ID  - 10.64898/2026.09.23.753846
ER  -