@misc{indiciaefe62eb6f9f7c, title = {Genomic Engineering of Gene Dosage: A Generalizable Framework for Modeling Haploinsufficiency-Mediated Human Disorders through Splicing Modulation}, author = {Smith, E. D. and Meisner, J. K. and Bullard, A. and Ward, C. B. and Licata, J. and Smith, C. and Kelly, C. M. and LaRochelle, Z. T. and Friedline, S. and Renberg, A. and Yucius, R. and Lange, J. and Hughes, E. D. and Saunders, T. L. and Freeman, Z. T. and Tsan, Y.-C. and Previs, M. J. and Kitzman, J. O. and Helms, A. S.}, year = {2026}, doi = {10.64898/2026.09.20.753023}, url = {https://www.biorxiv.org/content/10.64898/2026.09.20.753023v1}, note = {Source identifier: 10.64898/2026.09.20.753023} }