TY - RPRT TI - Pharmacological BET Protein Inhibition Reverts Niemann-Pick Type C Disease-Associated Changes in Human iPSC-Derived Cortical Neurons AU - Benigni, F. AU - Parente, M. AU - Marioli, C. AU - Borghi, R. AU - Cicolani, N. AU - Barthelemy, A. AU - Petrini, S. AU - Tartaglia, M. AU - Pfrieger, F. AU - Pallottini, V. AU - Compagnucci, C. PY - 2026 DO - 10.64898/2026.08.31.747771 UR - https://www.biorxiv.org/content/10.64898/2026.08.31.747771v1 ID - 10.64898/2026.08.31.747771 ER -