@misc{indiciae136819eb96c3, title = {A mutation-agnostic and allele-specific ASO strategy demonstrates potent functional rescue and retinal preservation in RHO-linked retinitis pigmentosa}, author = {Spaag, S. and Wu, W.-H. and Yun, J. and Winogrodzki, T. and Knudsen, A. S. and Fuso, M. and Stingl, K. and Komissarov, G. and Armento, A. and Baumann, B. and Kuehlewein, L. and Ayuso, C. and Fernandez-Caballero, L. and Collin, R. and Corradi, Z. and Roosing, S. and Kaltak, M. and Lochmann, C. and Radboudumc, F. and Banfi, S. and Karali, M. and Bolz, S. and Simonelli, F. and Dave, K. and Kohl, S. and Zrenner, E. and Demirkol, A. and Achberger, K. and Wissinger, B. and Tsang, S. H. and De Angeli, P.}, year = {2026}, doi = {10.64898/2026.08.25.747013}, url = {https://www.biorxiv.org/content/10.64898/2026.08.25.747013v1}, note = {Source identifier: 10.64898/2026.08.25.747013} }