TY  - RPRT
TI  - Adenine base editing correction of LMNA c.745C>T (p.R249W) in congenital muscular dystrophy myoblasts improves cellular phenotype while revealing deleterious p.L248P bystander effects
AU  - Santafe, M.
AU  - Hernandez, I.
AU  - Mazzeo, D.
AU  - Gomez-Dominguez, D.
AU  - Megias, D.
AU  - Perez de Castro, I.
PY  - 2026
DO  - 10.64898/2026.08.03.742539
UR  - https://www.biorxiv.org/content/10.64898/2026.08.03.742539v1
ID  - 10.64898/2026.08.03.742539
ER  -