@misc{indiciaec92c0aedcf5c, title = {CD117 epitope-shielded hematopoietic stem cell transplantation with toxin-free conditioning and in vivo selection ameliorates β-thalassemia model}, author = {Marone, R. and Lepore, R. and Paschoudi, K. and Zuin, J. and Sinopoli, A. and Camus, A. and Burgold, T. and Bartoszek, E. and Calabrese, D. and Toranelli, M. and Wittwer, J. and Rhiel, M. and Andrieux, G. and Li, C. and Hsu, A. and Wiederkehr, A. and Wellinger, L. C. and Grossjohann, E.-M. and Ten Buren, E. and Brault, J. and Garcia Prat, L. and Lehmann, F. and Do Sacramento, V. and Christopher Divsalar, C. and Yumlu, S. and Liu, D. R. and Lieber, A. and Cathomen, T. and Cornu, T. I. and Yannaki, E. and Stefanie Urlinger, S. and Jeker, L. T.}, year = {2026}, doi = {10.64898/2026.07.07.736903}, url = {https://www.biorxiv.org/content/10.64898/2026.07.07.736903v1}, note = {Source identifier: 10.64898/2026.07.07.736903} }