@misc{indiciae24010ae3416c, title = {Preclinical translation of Neurofibromatosis type 1 (NF1) exon 17 skipping using targeted U7-SnRNA packaged into engineered AAV serotypes.}, author = {Moore, M. and Rayat-Sanati, K. and Zhang, X. and Liu, H. and Rostamitehrani, Z. and Vijayasarathy, T. and Westin, E. and Esteves, M. and Maguire, C. A. and Kesterson, R. A. and Popplewell, L. and Wallis, D.}, year = {2026}, doi = {10.64898/2026.06.29.734312}, url = {https://www.biorxiv.org/content/10.64898/2026.06.29.734312v1}, note = {Source identifier: 10.64898/2026.06.29.734312} }