TY  - RPRT
TI  - Correction of a recurrent pathogenic variant in methylmalonic acidemia using adenine base editing
AU  - Kahn, E. M.
AU  - Said, H.
AU  - Qu, P.
AU  - Alameh, M.-G.
AU  - Wang, X.
AU  - Musunuru, K.
AU  - Ahrens-Nicklas, R. C.
PY  - 2026
DO  - 10.64898/2026.03.12.711365
UR  - https://www.biorxiv.org/content/10.64898/2026.03.12.711365v1
ID  - 10.64898/2026.03.12.711365
ER  -