@misc{indiciaee53a7a6fc51f, title = {Preclinical validation of AAV9-TECPR2 gene therapy in a novel knock-in model of TECPR2-related disorder}, author = {Lenfers Turnes, B. and Casey-Caplan, P. and Mejia, L. and Berry, T. and Zhao, J. and Villa, F. and Cropper, E. and Arab, M. and Zhang, B. and Surin, D. and Ebrahimi-Fakhari, D. and de Lima, S. and Kopin, A. and Andrews, N. and Hodgson, N. and Fagiolini, M.}, year = {2026}, doi = {10.64898/2026.03.02.708636}, url = {https://www.biorxiv.org/content/10.64898/2026.03.02.708636v1}, note = {Source identifier: 10.64898/2026.03.02.708636} }