@misc{indiciae5c52c322dd10, title = {ELP1 Gene Augmentation Restores Visual Function in a Mouse Model of Familial Dysautonomia}, author = {Cheng, H.-C. and Koli, S. and Lewis, K. and Anvarinia, Y. and Liu, Y. and Erdoes, M. and Keiper, C. E. and Estelien, R. and Chagnon, M. and Vandenberghe, L. H. and Gao, D. and Lefcort, F. and Morini, E. and Slaugenhaupt, S. A. and Chekuri, A.}, year = {2026}, doi = {10.64898/2026.01.09.698339}, url = {https://www.biorxiv.org/content/10.64898/2026.01.09.698339v1}, note = {Source identifier: 10.64898/2026.01.09.698339} }