@misc{indiciaef6ea95fabb50, title = {Treatment of Huntington's disease with a pan-HTT-targeting CRISPR nuclease}, author = {Tan, K. and Del Bosque Siller, D. and Xiong, A. Y. and Wang, A. X. A. and McCallister, T. X. and Mummadi, S. and St John, L. A. and Lee, T. K. and Carrillo, A. and Renshaw, D. G. and Zhou, R. H. and Lim, C. K. W. and He, J. and Fields, C. J. and Hayden, M. R. and Gaj, T.}, year = {2025}, doi = {10.64898/2025.12.20.695720}, url = {https://www.biorxiv.org/content/10.64898/2025.12.20.695720v1}, note = {Source identifier: 10.64898/2025.12.20.695720} }