@misc{indiciae8021670cc407,
  title = {Modulating splicing in five prime untranslated regions to treat rare haploinsufficient disease},
  author = {Beer Wells, E. S. and De Conti, L. and Kim, H. C. and Rohani, N. and Chundru, V. K. S. and Watts, L. M. and Dawes, R. and Chen, Y. and Martin-Geary, A. C. and Griffiths, M. J. and Scott, S. and Bamford, R. and Mill, J. and Wright, C. and Baralle, M. and Sanders, S. J. and Whiffin, N.},
  year = {2025},
  doi = {10.64898/2025.12.07.692584},
  url = {https://www.biorxiv.org/content/10.64898/2025.12.07.692584v1},
  note = {Source identifier: 10.64898/2025.12.07.692584}
}