@misc{indiciaee8e8b9562daa, title = {Nucleoside-Modified mRNA Encoding Alpha-Galactosidase A Reverses Fabry Disease Phenotypes in Human IPSC-Derived Cardiomyocytes}, author = {Juchem, M. and Ersoy, S. and Oehlsen, L. and Ye, J. L. and Weber, N. and Xiao, K. and Jahn, C. and Eggenschwiler, R. and Cantz, T. and Beimdiek, J. and Buettner, F. F. R. and Kraft, T. and Hegermann, J. and Bär, C. and Hoepfner, J. and Thum, T.}, year = {2025}, doi = {10.64898/2025.12.03.692072}, url = {https://www.biorxiv.org/content/10.64898/2025.12.03.692072v1}, note = {Source identifier: 10.64898/2025.12.03.692072} }