TY  - RPRT
TI  - AAV-mediated gene augmentation therapy restores critical functions in mutant iPSC-derived PRPF31+/- cells.
AU  - Brydon, E.
AU  - Bronstein, R.
AU  - Buskin, A.
AU  - Lako, M.
AU  - Pierce, E. A.
AU  - Fernandez-Godino, R.
PY  - 2019
DO  - 10.1101/729160
UR  - https://www.biorxiv.org/content/10.1101/729160v1
ID  - 10.1101/729160
ER  -