@misc{indiciae3d40e54f9744, title = {AAV-mediated gene augmentation therapy restores critical functions in mutant iPSC-derived PRPF31+/- cells.}, author = {Brydon, E. and Bronstein, R. and Buskin, A. and Lako, M. and Pierce, E. A. and Fernandez-Godino, R.}, year = {2019}, doi = {10.1101/729160}, url = {https://www.biorxiv.org/content/10.1101/729160v1}, note = {Source identifier: 10.1101/729160} }