@misc{indiciaef375d5d6dfe6, title = {Patient-Specific Midbrain Organoids with CRISPR Correction Reveal Disease Mechanisms and Enable Therapeutic Evaluation in Neuronopathic Gaucher Disease}, author = {Lin, Y. and Liou, B. and Fannin, V. and Adler, S. and Mayhew, C. N. and Hammonds, J. E. and Hu, Y.-C. and Tchieu, J. and Zhang, W. and Zhao, X. and Beres, R. L. and Setchell, K. D. and Kaynak, A. and Qi, X. and Feldman, R. A. and Sun, Y.}, year = {2025}, doi = {10.1101/2025.11.06.686937}, url = {https://www.biorxiv.org/content/10.1101/2025.11.06.686937v1}, note = {Source identifier: 10.1101/2025.11.06.686937} }