TY  - RPRT
TI  - Symptomatic treatment by a BBB-permeable AAV engineered to restore TDP-43 function slows motor neuron disease and prevents paralysis
AU  - Peethambaran Mallika, A.
AU  - Yu, J.
AU  - Sitzman, O.
AU  - Baghel, M. S.
AU  - Renganathan, S.
AU  - Sinha, I. R.
AU  - Melnikova, T.
AU  - Ling, J. P.
AU  - Wong, P. C.
PY  - 2025
DO  - 10.1101/2025.08.14.670400
UR  - https://www.biorxiv.org/content/10.1101/2025.08.14.670400v1
ID  - 10.1101/2025.08.14.670400
ER  -