TY - RPRT TI - Next Generation AAV-F Capsid gene therapy rescues disease pathology in a model of Pyruvate Dehydrogenase Complex Deficiency AU - Keegan, A. AU - Cetin, O. AU - Chilcott, E. M. AU - Antinao Diaz, J. F. AU - Eaton, S. AU - Waddington, S. N. AU - Counsell, J. R. AU - Rahman, S. AU - Karda, R. PY - 2025 DO - 10.1101/2025.07.30.667478 UR - https://www.biorxiv.org/content/10.1101/2025.07.30.667478v1 ID - 10.1101/2025.07.30.667478 ER -