@misc{indiciae367b037ae162, title = {A Compact Base Editor Rescues AATD-associated Liver and Lung Disease in Mouse Models}, author = {Gao, J. and Bamidele, N. and Pires-Ferreira, D. and Destefano, A. and Tang, Q. and Cao, Y. and Xie, J. and Gao, G. and Gruntman, A. and Sontheimer, E. and Flotte, T. and Xue, W. J.}, year = {2025}, doi = {10.1101/2025.05.07.652636}, url = {https://www.biorxiv.org/content/10.1101/2025.05.07.652636v1}, note = {Source identifier: 10.1101/2025.05.07.652636} }