@misc{indiciae07137ef83544, title = {Atrophin-1 Antisense Oligonucleotide Provides Robust Protection from Pathology in a Fully Humanized DRPLA Model}, author = {Smith, V. L. and Gidi, B. Z. and Bragg, R. M. and Cantle, J. P. and Ben-Varon, A. and Nobel, B. and Prades, S. and Compton, A. and Greenfield, J. and Korecka-Roet, J. and Yu, T. and Khurana, V. and Kordasiewicz, H. B. and Zhao, H. T. and Barker-Haliski, M. and Child, D. D. and Carroll, J. B.}, year = {2025}, doi = {10.1101/2025.03.18.643143}, url = {https://www.biorxiv.org/content/10.1101/2025.03.18.643143v1}, note = {Source identifier: 10.1101/2025.03.18.643143} }