@misc{indiciae900176be2cef, title = {Gene Editing for ATXN3 Inactivation in Machado-Joseph disease: CRISPR-Cas9 as a Therapeutic Alternative to TALEN-Induced Toxicity}, author = {Lopes, S. M. and Lopes, M. M. and Oliveira, D. and Santana, M. M. and Fernandes, A. R. and Vasconcelos-Ferreira, A. and Pereira, D. and Casquinha, M. and Nobrega, C. and Matos, C. A. and Sanjana, N. E. and Hsu, P. D. and Ran, F. A. and Swiech, L. and Cong, L. and Zhang, F. and Nobre, R. J. and de Almeida, L. P.}, year = {2025}, doi = {10.1101/2025.02.14.637261}, url = {https://www.biorxiv.org/content/10.1101/2025.02.14.637261v1}, note = {Source identifier: 10.1101/2025.02.14.637261} }