TY - RPRT TI - Lipid-based nanoparticles deliver mRNA to reverse the pathogenesis of lysosomal acid lipase deficiency in a preclinical model AU - Zadory, M. AU - Lopez-Vince, E. AU - Haddouch, H. AU - Babity, S. AU - Rezaei, N. AU - Moawad, F. AU - Kenaan El Rahbani, R. M. AU - Vujic, N. AU - Kratky, D. AU - Gravel, S.-P. AU - Brambilla, D. PY - 2024 DO - 10.1101/2024.12.07.627318 UR - https://www.biorxiv.org/content/10.1101/2024.12.07.627318v1 ID - 10.1101/2024.12.07.627318 ER -