TY - RPRT TI - Engineered CRISPR-Base Editors as a Permanent Treatment for Familial Dysautonomia AU - Yun, S. AU - Chekuri, A. AU - Art, J. AU - Kondabolu, K. AU - Slaugenhaupt, S. A. AU - Zeltner, N. AU - Kleinstiver, B. P. AU - Morini, E. AU - Alves, C. R. R. PY - 2024 DO - 10.1101/2024.11.27.625322 UR - https://www.biorxiv.org/content/10.1101/2024.11.27.625322v1 ID - 10.1101/2024.11.27.625322 ER -