@misc{indiciae6fd95f2d0e5f, title = {Optimization of systemic AAV9 gene therapy in Niemann-Pick disease type C1 mice}, author = {Mylvara, A. V. and Gibson, A. L. and Gu, T. and Davidson, C. D. and Incao, A. A. and Melnyk, K. and Pierre-Jacques, D. and Cologna, S. M. and Venditti, C. P. and Porter, F. and Pavan, W. J.}, year = {2024}, doi = {10.1101/2024.06.07.597901}, url = {https://www.biorxiv.org/content/10.1101/2024.06.07.597901v1}, note = {Source identifier: 10.1101/2024.06.07.597901} }