@misc{indiciae0eb445c5a1be, title = {Development and IND-enabling studies of a novel Cas9 genome-edited autologous CD34+ cell therapy to induce fetal hemoglobin for sickle cell disease}, author = {Katta, V. and O'Keefe, K. and Li, Y. and Mayuranathan, T. and Levine, R. M. and Lazzarotto, C. R. and Wood, R. K. and Powers, A. and Mayberry, K. and Manquen, G. and Yao, Y. and Zhang, J. and Jang, Y. and Nimmagadda, N. and Dempsey, E. A. and Lee, G. and Uchida, N. and Cheng, Y. and Fazio, F. and Lockey, T. and Meagher, M. and Sharma, A. and Tisdale, J. F. and Zhou, S. and Yen, J. S. and Weiss, M. J. and Tsai, S. Q.}, year = {2024}, doi = {10.1101/2024.04.30.591737}, url = {https://www.biorxiv.org/content/10.1101/2024.04.30.591737v1}, note = {Source identifier: 10.1101/2024.04.30.591737} }