TY - RPRT TI - Dose escalation pre-clinical trial of novel Dok7-AAV in mouse model of DOK7 congenital myasthenia AU - Cossins, J. A. AU - Kozma, I. AU - Canzonetta, C. AU - Hawkins, A. AU - Beeson, D. AU - Sepulveda, P. AU - Dong, Y. PY - 2024 DO - 10.1101/2024.02.09.579626 UR - https://www.biorxiv.org/content/10.1101/2024.02.09.579626v1 ID - 10.1101/2024.02.09.579626 ER -