TY - RPRT TI - CRISPR/Cas9-based disease modelling and functional correction of Interleukin 7 Receptor alpha Severe Combined Immunodeficiency in T-lymphocytes and hematopoietic stem cells AU - Rai, R. AU - Steinberg, Z. AU - Romito, M. AU - Zinghirino, F. AU - Hu, Y.-T. AU - White, N. AU - Naseem, A. AU - Thrasher, A. J. AU - Turchiano, G. AU - Cavazza, A. PY - 2023 DO - 10.1101/2023.11.07.566043 UR - https://www.biorxiv.org/content/10.1101/2023.11.07.566043v1 ID - 10.1101/2023.11.07.566043 ER -