TY - RPRT TI - Robust nuclease-dead S. aureus dCas9-mediated alpha-synuclein knockdown in substantia nigra in a humanized mouse model of Parkinson's disease AU - Torres, C. A. M. AU - Zafar, F. AU - Sastre, D. AU - Hermesky, D. AU - Chen, M. Y. AU - Vazquez, J. P. AU - Qi, L. S. AU - Kirik, D. AU - Schùˆle, B. PY - 2023 DO - 10.1101/2023.09.05.556425 UR - https://www.biorxiv.org/content/10.1101/2023.09.05.556425v1 ID - 10.1101/2023.09.05.556425 ER -