@misc{indiciae75c17fb4fed3, title = {CTNS mRNA as a potential treatment for nephropathic cystinosis}, author = {Bondue, T. and Berlingerio, S. P. and Siegerist, F. and Sendino-Garvi, E. and Schindler, M. and Cairoli, S. and Goffredo, B. M. and Arcolino, F. O. and Dieker, J. and Janssen, M. and Endlich, N. and Brock, R. and Gijsbers, R. and van den Heuvel, L. and Levtchenko, E.}, year = {2023}, doi = {10.1101/2023.04.28.538106}, url = {https://www.biorxiv.org/content/10.1101/2023.04.28.538106v1}, note = {Source identifier: 10.1101/2023.04.28.538106} }