TY - RPRT TI - CRISPRa-induced upregulation of human LAMA1 compensates for LAMA2-deficiency in Merosin-deficient congenital muscular dystrophy AU - Arockiaraj, A. I. AU - Johnson, M. A. AU - Munir, A. AU - Ekambaram, P. AU - Lucas, P. C. AU - Mcallister-Lucas, L. AU - Kemaladewi, D. U. PY - 2023 DO - 10.1101/2023.03.06.531347 UR - https://www.biorxiv.org/content/10.1101/2023.03.06.531347v1 ID - 10.1101/2023.03.06.531347 ER -