@misc{indiciae2fb689df48df, title = {Exon 44 skipping in Duchenne muscular dystrophy: NS-089/NCNP-02, a dual-targeting antisense oligonucleotide}, author = {Watanabe, N. and Tone, Y. and Nagata, T. and Masuda, S. and Saito, T. and Motohashi, N. and Takagaki, K. and Aoki, Y. and Takeda, S.}, year = {2023}, doi = {10.1101/2023.02.23.529798}, url = {https://www.biorxiv.org/content/10.1101/2023.02.23.529798v1}, note = {Source identifier: 10.1101/2023.02.23.529798} }