@misc{indiciae17ab0f1b8e21, title = {Development of a novel oral treatment that rescues gait ataxia and retinal degeneration in a phenotypic mouse model of familial dysautonomia.}, author = {Morini, E. and Chekuri, A. and Logan, E. and Bolduc, J. and Kirchner, E. and Salani, M. and Krauson, A. and Narasimhan, J. and Gabbeta, V. and Grover, S. and Dakka, A. and Mollin, A. and Jung, S. and Zhao, X. and Zhang, N. and Zhang, S. and Arnold, M. and Woll, M. and Naryshkin, N. and Weetall, M. and Slaugenhaupt, S.}, year = {2022}, doi = {10.1101/2022.11.04.515198}, url = {https://www.biorxiv.org/content/10.1101/2022.11.04.515198v1}, note = {Source identifier: 10.1101/2022.11.04.515198} }