@misc{indiciae6f21dd497e8d, title = {Angelman syndrome patient neuron screen identifies a potent and selective clinical ASO targeting UBE3A-ATS with long lasting effect in cynomolgus monkey}, author = {Jagasia, R. and Bon, C. and Rasmussen, S. V. and Badillo, S. and Tehler, D. and Buchy, D. and Berrera, M. and Prasad, M. and Terrigno, M. and Pandya, N. J. and Costa, V. and Wang, C. and Pedersen, L. and Miller, M. T. and Dumong Erichsen, K. and Joenson, L. and Hipp, J. and Bonni, A. and Mueller, L. and Braendli-Baiocco, A. and Kremer, T. and Koller, E. and Hoener, M.}, year = {2022}, doi = {10.1101/2022.06.09.495066}, url = {https://www.biorxiv.org/content/10.1101/2022.06.09.495066v1}, note = {Source identifier: 10.1101/2022.06.09.495066} }