TY - RPRT TI - Bayesian modeling and simulation to inform rare disease drug development early decision-making: application to Duchenne muscular dystrophy AU - Lennie, J. AU - Mondick, J. T. AU - Gastonguay, M. R. PY - 2021 DO - 10.1101/2021.02.05.429907 UR - https://www.biorxiv.org/content/10.1101/2021.02.05.429907v1 ID - 10.1101/2021.02.05.429907 ER -