@misc{indiciae9046a4efedb6,
  title = {Bayesian modeling and simulation to inform rare disease drug development early decision-making: application to Duchenne muscular dystrophy},
  author = {Lennie, J. and Mondick, J. T. and Gastonguay, M. R.},
  year = {2021},
  doi = {10.1101/2021.02.05.429907},
  url = {https://www.biorxiv.org/content/10.1101/2021.02.05.429907v1},
  note = {Source identifier: 10.1101/2021.02.05.429907}
}