TY - RPRT TI - Exon 13-skipped USH2A protein retains functional integrity in mice, suggesting an exon skipping therapeutic approach to treat USH2A-associated disease. AU - Pendse, N. AU - Lamas, V. AU - Maeder, M. AU - Pawlyk, B. AU - Gloskowski, S. AU - Pierce, E. A. AU - Chen, Z.-Y. AU - Liu, Q. PY - 2020 DO - 10.1101/2020.02.04.934240 UR - https://www.biorxiv.org/content/10.1101/2020.02.04.934240v1 ID - 10.1101/2020.02.04.934240 ER -