TY - RPRT TI - Targeted gene correction of FKRP by CRISPR/Cas9 restores functional glycosylation of α-dystroglycan in cortical neurons derived from human induced pluripotent stem cells AU - Lana, B. AU - Kim, J. AU - Ryan, D. AU - Konstantinidis, E. AU - Louzada, S. AU - Fu, B. AU - Yang, F. AU - Stemple, D. L. AU - Liu, P. AU - Muntoni, F. AU - Lin, Y.-Y. PY - 2017 DO - 10.1101/101352 UR - https://www.biorxiv.org/content/10.1101/101352v1 ID - 10.1101/101352 ER -